Targeted insertion of partial CFTR cDNA replicates native CF…

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Targeted insertion of partial CFTR cDNA replicates native CFTR expression with restored channel function in CF airway epithelium

Article 2026 EN Gold

integration via other editing and delivery methodologies.

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UN Sustainable Development Goals
1 SDGs
Authors & Affiliations
23 authors
#AuthorInstitutionsORCID
1 Cristina Barillá University of Alabama at Birmi… (US) The University of Texas Health… (US)
2 Shingo Suzuki University of Alabama at Birmi… (US) The University of Texas Health… (US)
3 So Hyun Park Rice University (US) —
4 D. Nalluri University of Alabama at Birmi… (US) —
5 Hui Wen University of Alabama at Birmi… (US) —
6 Mohamed A. Hanafy University of Alabama at Birmi… (US) —
7 Daniel Betancourth Rice University (US) —
8 Ayushi Umrigar Case Western Reserve Universit… (US) —
9 Shih‐Hsing Leir Case Western Reserve Universit… (US)
10 Katreya Lovrenert Case Western Reserve Universit… (US)
11 Andrey Sivachenko Cystic Fibrosis Foundation (US)
12 Barbara Tabak Cystic Fibrosis Foundation (US) —
13 Zhong Liu University of Alabama at Birmi… (US) —
14 Rui Zhao University of Alabama at Birmi… (US)
15 Hillary C. Valley Cystic Fibrosis Foundation (US) —
16 András Rab Emory University (US)
17 Eric J. Sorscher Emory University (US)
18 George M. Solomon University of Alabama at Birmi… (US) —
19 Martin Mense Cystic Fibrosis Foundation (US)
20 John P. Carulli Cystic Fibrosis Foundation (US)
21 Ann Harris Case Western Reserve Universit… (US)
22 Gang Bao Rice University (US) —
23 Brian R. Davis University of Alabama at Birmi… (US) The University of Texas Health… (US)

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